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Recent advancements in exon-skipping therapies using antisense oligonucleotides and genome editing for the treatment of various muscular dystrophies
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- Journal:
- Expert Reviews in Molecular Medicine / Volume 21 / 2019
- Published online by Cambridge University Press:
- 02 October 2019, e5
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Genetic Myopathies Initially Diagnosed and Treated as Inflammatory Myopathy
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- Journal:
- Canadian Journal of Neurological Sciences / Volume 43 / Issue 3 / May 2016
- Published online by Cambridge University Press:
- 25 February 2016, pp. 381-384
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